Case studies

Changing the future of personalised paediatric care together

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Featured Case Study

Preparing and supporting children undergoing gene therapy

Family-25

Background

Little Journey partnered with a global pharmaceutical company to tailor our support solution for children with Duchenne Muscular Dystrophy (DMD) participating in gene therapy research.

Challenges

 Screening & enrolment 

Gene therapy research presents unique challenges in screening and enrolment. Families pin their hope on the potential treatment, but not all will meet the inclusion criteria.

 Engagement & retention 

Retaining participants during the monitoring phase is vital for successful data collection. However, this period brings uncertainty for families, who may worry about adverse events, effectiveness, and disruption to their child's life.

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 NEWS 

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Find out about our recent accessibility improvements and what's coming next

We’re committed to supporting all children to better health. As part of this, we're making some key accessibility updates to enhance families’ experience.

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 ACCESSIBILITY STATEMENT 

Here's where you can read our accessibility statement 

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 BLOG 

All about Little Journey's Accessibility Centre of Excellence

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 Vaccines 

 

Little Journey scientist character in her lab

Reaching 500,000 people with children's COVID-19 vaccine and testing education videos

NHS Digital, Public Health England, and NHS Test and Trace partnered with Little Journey to develop engaging content to explain COVID-19 vaccines and testing.

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 Rare Disease 

 

Bella Family

Preparing and supporting children undergoing gene therapy

Little Journey partnered with a global pharmaceutical company to tailor our support solution for children with Duchenne Muscular Dystrophy (DMD) participating in gene therapy research.

Read more

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Whitepaper

Solomon & Play
Healthcare

The Benefits of Play in Healthcare Environments

In our latest whitepaper, we focus on the long-established benefits of play within healthcare settings, highlighting how providing children with information about their healthcare journey in playful ways, along with them sharing their strengths and needs, that healthcare experiences will be significantly improved for all.